Drug Development Pipeline

All information shared on this website is publicly available and reproduced here as a resource for the community. Note that FARA does not endorse, control, or govern the research pipeline programs.

The pipeline is a visual tool for communicating the progress of potential therapeutics.

To download a printable PDF of the pipeline, click here. Lead candidates are grouped based on mechanism of action or approach to treatment. The stage of the research (in the country where the candidate is furthest in its development process) is represented across the page. To learn more about the stages of drug development, click here.

FARA supports the advancement of treatments with financial resources, advocacy, patient engagement and/or fostered collaboration. FARA believes that an effective treatment for FA will come in the form of a "cocktail approach" — a combination of two or more therapies. The descriptions of programs shared here are for informational purposes only and are not medical advice or an endorsement of any program.

Active – programs currently under development and supported by the listed sponsor.

Inactive – programs no longer in development because of lack of safety or efficacy or for which the sponsor has paused recruitment because of resource constraints and for which there is not a clear path forward.