Postdoctoral Research Award | Outcome Measures & Biomarkers
Funded Grants
FARA Funded Research Grants
General Research Grant | Gene & Stem Cell Therapy
Characterization of ocular phenotype of the YG8-800 mouse model of FA and retinal-targeted treatment by AAV based CRISPR-Cas9 gene editing
Postdoctoral Research Award | Mechanism or Pathway of Disease
Unraveling Epigenetic Mechanisms and Therapeutic Strategies for FXN Silencing in Friedreich’s Ataxia
General Research Grant | Gene & Stem Cell Therapy
Rescuing frataxin expression by alternative splicing reprogramming with base editing
General Research Grant | Gene & Stem Cell Therapy
Application of RSwitch technology to improve Friedreich’s ataxia viral gene therapy safety and efficacy: control of FXN transgene expression through a small molecule regulation
Award for Innovative Mindset (AIM) | Gene & Stem Cell Therapy
Development of Epigenetic Editors for Frataxin Reactivation
General Research Grant | Outcome Measures & Biomarkers
Quantifying sitting balance in children and adults with Friedreich ataxia – development of clinical and instrumented measures
Postdoctoral Fellowship | Mechanism or Pathway of Disease
Design and synthesis of SynGR library to probe into the role of NSD-2,3 proteins in FXN expression in FRDA
Bronya J. Keats Research Collaboration Award | Improving Clinical Outcomes
Impact of cerebellar transcranial direct current stimulation on FA brain and cerebellar neurophysiological fingerprints and on clinical symptoms assessed by multimodal evaluations
Postdoctoral Fellowship | Mechanism or Pathway of Disease
Understanding the Pathogenesis of Friedreich’s Ataxia by Single-Cell Integration of Gene Expression, Epigenetics and Connectivity in the Cerebellar Nuclei
Postdoctoral Research Award | Gene & Stem Cell Therapy
Enhancing Gene Therapy Delivery to the Brain via Human Blood-Brain Barrier Receptors
Graduate Research Fellowship | Gene & Stem Cell Therapy