Drug Development Pipeline

The pipeline is a visual tool for communicating the progress of potential therapeutics.

To download a printable PDF of the pipeline, click here.

Lead candidates are grouped based on mechanism of action or approach to treatment. The horizontal axis indicates the stage of the research (in the country where the candidate is furthest in its development process).

FARA supports the advancement of treatments with financial resources, advocacy, patient engagement and/or fostered collaboration. FARA believes that an effective treatment for FA will come in the form of a “cocktail approach” — a combination of two or more therapies. The descriptions of programs shared here are for informational purposes only and are not medical advice or an endorsement of any program.

To learn more about the stages of drug development, click here.