News & Blog

Meet The Community: Jakub

Meet The Community: Morgan Talevich

Stealth BioTherapeutics Receives Orphan Drug Designation from FDA for Elamipretide for the Treatment of Friedreich’s Ataxia

Meet The Community: Fatbardha Nuzi

Meet The Community: AJ Perez

Meet The Community: Denise Votta

Design Therapeutics Announces FDA Clearance of Investigational New Drug Application for First GeneTAC™ Molecule for Friedreich Ataxia

Meet The Community: Britanie Sutton

Lexeo Announces FDA Clearance of IND Application for LX2006 for Friedreich’s Ataxia Cardiomyopathy

Meet The Community: Richie Currier

Larimar Therapeutics Provides Update on CTI-1601 Clinical Program

Meet The Community: Ali