News & Blog
News & Blog
Design Therapeutics Initiated Phase 1 Single Ascending Dose Trial of DT-216P2 in Healthy Volunteers
2025 Runway to the Cure Recap
Meet the Community: Sienna Helms
FA Community Statement from Biogen
Giving Back Through Surgical Tissue Donation by Jake Juip
Press Release & Community Statement: PTC Therapeutics Announces FDA Acceptance and Priority Review for Vatiquinone NDA for the Treatment of Children and Adults with Friedreich’s Ataxia
February 2025 – Advocacy Newsletter
Job Posting: Development Manager (Major Gifts)
Meet the Community 2: A Closer Look – Matthew LaFleur
Letter to the FA Community from Astellas Pharma
